Scientists have developed a novel approach of genome editing to repair muscle stem (satellite) cells, offering new hope for ...

Muscular dystrophies are mostly hereditary disorders clinically manifested by progressive muscle wasting and weakness, and pathologically by muscle degeneration and necrosis. 1 Among them, Duchenne ...

为解决杜氏肌营养不良症（DMD）照护者因照护负担对职业发展及工作生产力造成的具体影响问题，研究人员开展了一项横断面调查。结果显示，照护者平均每日花费8小时照护，77%的照护者因照护责任经历了至少一次工作调整，工作生产力损失达35%。该研究为理解DMD照护者的社会经济负担提供了当代、美国本土化的具体数据。

A Community Event for Duchenne Muscular Dystrophy Awareness Brick, United States – January 1, 2026 / Steps for Hope 5K / The ...

The US Food and Drug Administration has given the green light for the first gene therapy that treats a rare form of muscular dystrophy to be used in most people who have the disease and a certain ...

The FDA cited risk of IV infection and kidney toxicity in its letter. The company's CEO said the FDA issued no prior warning for the two concerns.

When Elie and Nancy Eid founded Save Our Sons Duchenne Foundation in 2008 after their first-born son Emilio was diagnosed with Duchenne muscular dystrophy, they could never have imagined how ...

In human biology, the protein dystrophin is a shining example of Joni Mitchell’s classic line, “you don’t know what you’ve got ’til it’s gone.” Dystrophin stabilizes muscle cells. In its absence, the ...

Solid Biosciences Inc. (NASDAQ:SLDB) is one of the stocks that will double in 2026. On December 4, Needham analyst Gil Blum initiated coverage of Solid Biosciences with a Buy rating and $16 price ...

Duchenne muscular dystrophy (DMD) is the most common muscle disease in children and is passed on by X-linked recessive inheritance. Characteristic is a progressive muscular atrophy. Researchers have ...

Deb and Shawn Jenssen were used to frustration. Their kids had been turned away from studies. Doctors had questioned if they could really be showing signs of a disease even as it made it harder for ...

Becker muscular dystrophy (BMD) is a type of muscular dystrophy, a genetic condition that weakens and damages muscles. It can worsen with age. However, its symptoms are less severe than those of ...